One-year safety and efficacy of mitapivat in sickle cell disease
Myrthe J van Dijk, Minke A E Rab, Brigitte A van Oirschot, Jennifer Bos, Cleo Derichs, Anita W Rijneveld, Marjon H Cnossen, Erfan Nur, Bart J Biemond, Marije Bartels, Judith J M Jans, W W van Solinge, Roger E G Schutgens, Richard van Wijk, Eduard J van Beers
Blood Advances, 2023, vol. 7, p.7539-7550